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Temp: Repair of ELANE therapeutic gene editing for congenital neutropenia
Therapeutic Gene Editing for Severe Congenital Neutropenia
Background
Severe congenital neutropenia (SCN) is a rare inherited disorder characterized by low absolute neutrophil counts which increases the risk of life-threatening infections. Occurrence of SCN is attributed to changes in various genes, but an estimated 50% of severe congenital...
Published: 3/26/2026
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Updated: 4/11/2024
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Inventor(s): Daniel Bauer, Scot Wolfe, Peter Newburger, Josias Frazão, Shuquan Rao
Keywords(s):
Category(s): Technology Classifications > Invention Type > Therapeutics, Technology Classifications > Invention Type > Therapeutics > Gene Therapy, Technology Classifications > Disease Area > Rare Diseases
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