|
Compounds Treating AP-4 Associated Hereditary Spastic Paraplegia
Compounds Treating AP-4 Associated Hereditary Spastic Paraplegia
Background
Hereditary Spastic Paraplegia (HSP) is a group of inherited neurological disorders characterized by progressive spasticity, weakness, and gait abnormalities and affects approximately 5-10 per 100,000 individuals worldwide. Among its subtypes, Adaptor Protein Complex 4 (AP-4)-related...
Published: 3/23/2026
|
Updated: 7/28/2025
|
Inventor(s): Darius Ebrahimi-Fakhari, Mustafa Sahin, Masato Satoh, Jed Hubbs
Keywords(s): Hereditary Spastic Parapeligia, Movement Disorder, Neuromuscular Disorder
Category(s): Technology Classifications > Disease Area > Neurology, Technology Classifications > Disease Area > Rare Diseases, Technology Classifications > Invention Type > Therapeutics > Small Molecule
|
